Developing gene therapy for inherited retinal degenerations
<p>The aim of this thesis was to evaluate the efficacy and safety of retinal gene therapy in a pre-clinical model of CDHR1-associated retinal degeneration – a hitherto untreatable, blinding disorder.</p> <p>Deep phenotyping of the Cdhr1-/- murine model demonstrated severe early de...
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Format: | Thesis |
Language: | English |
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2022
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