Potential therapies using myogenic stem cells combined with bio-engineering approaches for treatment of muscular dystrophies

Muscular dystrophies (MDs) are a group of heterogeneous genetic disorders caused by mutations in the genes encoding the structural components of myofibres. The current state-of-the-art treatment is oligonucleotide-based gene therapy that restores disease-related protein. However, this therapeutic ap...

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Bibliographic Details
Main Authors: Motohashi, N, Shimizu-Motohashi, Y, Roberts, T, Aoki, Y
Format: Journal article
Language:English
Published: MDPI 2019