Delivery of large genomic DNA inserts >100 kb using HSV-1 amplicons.
The principal aim of gene therapy for recessive genetic diseases is to supplement the loss of function of an endogenous gene. For the treatment of many diseases regulation of transgene expression at physiological levels, expression of multiple splice variants, and correct tissue specificity are of u...
| Main Authors: | , |
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| Format: | Journal article |
| Language: | English |
| Published: |
2006
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