Genetic medicines for CF: Hype versus reality
Since identification of the CFTR gene over 25 years ago, gene therapy for cystic fibrosis (CF) has been actively developed. More recently gene therapy has been joined by other forms of "genetic medicines" including mRNA delivery, as well as genome editing and mRNA repair-based strategies....
| Main Authors: | , , , , , , , , , , |
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| Format: | Journal article |
| Sprog: | English |
| Udgivet: |
Wiley
2016
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