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  • REPEAT ADMINISTRATION OF GL67A...
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REPEAT ADMINISTRATION OF GL67A/PGM169 IS FEASIBLE, SAFE, AND PRODUCES ENDOGENOUS LEVELS OF CFTR EXPRESSION AFTER 12 DOSES

REPEAT ADMINISTRATION OF GL67A/PGM169 IS FEASIBLE, SAFE, AND PRODUCES ENDOGENOUS LEVELS OF CFTR EXPRESSION AFTER 12 DOSES

Bibliografiska uppgifter
Huvudupphovsmän: Alton, E, Boyd, A, Cheng, S, Davies, J, Davies, L, Dayan, A, Gill, DR, Griesenbach, U, Higgins, T, Hyde, S, Innes, A, McLachlan, G, Porteous, D, Pringle, I, Scheule, R, Sumner-Jones, S
Materialtyp: Conference item
Publicerad: 2012
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Liknande verk

  • Cumulative CFTR expression following repeated aerosol delivery of non-viral pGM169/GL67A formulation to mouse lung
    av: Alton, E, et al.
    Publicerad: (2012)
  • EVALUATION OF SAFETY AND GENE EXPRESSION WITH A SINGLE DOSE OF PGM169/GL67A ADMINISTERED TO THE NOSE AND LUNG OF INDIVIDUALS WITH CYSTIC FIBROSIS: THE UK CF GENE THERAPY CONSORTIUM "PILOT STUDY''
    av: Davies, J, et al.
    Publicerad: (2009)
  • EVALUATION OF SAFETY AND GENE EXPRESSION WITH A SINGLE DOSE OF PGM169/GL67A ADMINISTERED TO THE NOSE AND LUNG OF INDIVIDUALS WITH CF: THE UK CF GENE THERAPY CONSORTIUM "PILOT STUDY"
    av: Davies, J, et al.
    Publicerad: (2009)
  • Towards gene therapy for cystic fibrosis: Biodistribution of GL67A/pGM169 DNA and mRNA following aerosol delivery to the mouse lung
    av: Pringle, I, et al.
    Publicerad: (2008)
  • SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CF
    av: Davies, J, et al.
    Publicerad: (2011)

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