AAV2/2-CBA-REP1 Vector with WPRE Provides Functional Expression of the Transgene in Choroideremia Mouse Knock-Out and Patient Cells

Библиографические подробности
Главные авторы: Tolmachova, T, Tolmachov, O, Barnard, A, Groppe, M, During, M, MacLaren, R, Seabra, M
Формат: Conference item
Опубликовано: 2012