Pharmacotherapeutic strategies using small molecules for the treatment of glycolipid lysosomal storage disorders.
The glycolipid lysosomal storage diseases are a collection of rare, inherited disorders of metabolism associated with heterogeneous pathologies and reduced life expectancy. Reduction of the substrate that accumulates due to catabolic enzyme deficiency can be mediated by an increasing number of thera...
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| Formáid: | Journal article |
| Teanga: | English |
| Foilsithe / Cruthaithe: |
2007
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