AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy

Eitemau Tebyg

• AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy
  gan: Goyenvalle, A, et al.
  Cyhoeddwyd: (2011)
• Engineering exon-skipping vectors expressing U7 snRNA constructs for Duchenne muscular dystrophy gene therapy.
  gan: Goyenvalle, A, et al.
  Cyhoeddwyd: (2011)
• Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy
  gan: Goyenvalle, A, et al.
  Cyhoeddwyd: (2012)
• Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.
  gan: Goyenvalle, A, et al.
  Cyhoeddwyd: (2012)
• Upgrading U7snRNA To Complete Efficient Rescue of Dystrophin by Exon-Skipping in DMD Patients
  gan: Goyenvalle, A, et al.
  Cyhoeddwyd: (2009)