Towards the elucidation of the mechanism of action of small molecule upregulators of utrophin using chemical proteomics
<p>Duchenne Muscular Dystrophy (DMD) is an X-linked recessive and progressive muscle-wasting disease caused by a lack of the cytoskeletal protein dystrophin. There is currently no disease modifying treatment for all patients, although various promising approaches (e.g. exon skipping, read thro...
Main Author: | Vuorinen, A |
---|---|
Other Authors: | Russell, A |
Format: | Thesis |
Language: | English |
Published: |
2017
|
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