Gene Therapy for Choroideremia Using an Adeno-Associated Viral (AAV) Vector.
Choroideremia is an outer retinal degeneration with a characteristic clinical appearance that was first described in the nineteenth century. The disorder begins with reduction of night vision and gradually progresses to blindness by middle age. The appearance of the fundus in sufferers is recognizab...
| Main Authors: | , , |
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| Format: | Journal article |
| Language: | English |
| Published: |
2014
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