Visual acuity after retinal gene therapy for Choroideremia

Two recent clinical reports of retinal gene therapy with adeno-associated virus (AAV) vectors in patients with Leber’s congenital amaurosis showed initial gains in visual function that subsequently declined. We previously reported early improvement in visual acuity in two of six patients who receive...

Full description

Bibliographic Details
Main Authors: Edwards, T, Jolly, J, Groppe, M, Barnard, A, Cottriall, C, Tolmachova, T, Black, G, Webster, A, Lotery, A, Holder, G, Xue, K, Downes, S, Simunovic, M, Seabra, M, MacLaren, R
Format: Journal article
Language:English
Published: Massachusetts Medical Society 2016