Visual acuity after retinal gene therapy for Choroideremia

Two recent clinical reports of retinal gene therapy with adeno-associated virus (AAV) vectors in patients with Leber’s congenital amaurosis showed initial gains in visual function that subsequently declined. We previously reported early improvement in visual acuity in two of six patients who receive...

Disgrifiad llawn

Manylion Llyfryddiaeth
Prif Awduron: Edwards, T, Jolly, J, Groppe, M, Barnard, A, Cottriall, C, Tolmachova, T, Black, G, Webster, A, Lotery, A, Holder, G, Xue, K, Downes, S, Simunovic, M, Seabra, M, MacLaren, R
Fformat: Journal article
Iaith:English
Cyhoeddwyd: Massachusetts Medical Society 2016