Pharmacological strategies for muscular dystrophy.

Duchenne muscular dystrophy (DMD) is a fatal, genetic disorder whose relentless progression underscores the urgency for developing a cure. Although Duchenne initiated clinical trials roughly 150 years ago, therapies for DMD remain supportive rather than curative. A paradigm shift towards developing...

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Bibliographic Details
Main Authors: Khurana, T, Davies, K
Format: Journal article
Language:English
Published: 2003