Antisense oligonucleotide therapeutics in clinical trials for the treatment of inherited retinal diseases

<p>Introduction</p> <p>Antisense oligonucleotides (ASOs) represent a class of drugs which can be rationally designed to complement the coding or non-coding regions of target RNA transcripts. They could modulate pre-messenger RNA splicing, induce mRNA knockdown, or block translation...

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Bibliographic Details
Main Authors: Xue, K, MacLaren, RE
Format: Journal article
Language:English
Published: Taylor and Francis 2020