Pharmacological advances for treatment in Duchenne muscular dystrophy
Duchenne muscular dystrophy (DMD) is a lethal, X-linked muscle-wasting disease caused by lack of dystrophin, essential for muscle fibre integrity. Despite extensive pre-clinical studies, development of an effective treatment has proved challenging. More recently, significant progress has been made w...
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| Médium: | Journal article |
| Jazyk: | English |
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Elsevier
2017
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