Pharmacological advances for treatment in Duchenne muscular dystrophy

Duchenne muscular dystrophy (DMD) is a lethal, X-linked muscle-wasting disease caused by lack of dystrophin, essential for muscle fibre integrity. Despite extensive pre-clinical studies, development of an effective treatment has proved challenging. More recently, significant progress has been made w...

पूर्ण विवरण

ग्रंथसूची विवरण
मुख्य लेखकों: Guiraud, S, Davies, K
स्वरूप: Journal article
भाषा:English
प्रकाशित: Elsevier 2017