Oligonucleotide-based therapies for neuromuscular disease
<p>Genetic neuromuscular diseases remain essentially untreatable. Duchenne muscular dystrophy (DMD) is one such example and another is <em>C9ORF72</em>-related frontotemporal dementia/amyotrophic lateral sclerosis (c9FTD/ALS). Both these conditions may, however, be amenable to trea...
| Main Authors: | , |
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| Format: | Thesis |
| Language: | English |
| Published: |
2015
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| Subjects: |