Non-viral delivery of CRIPSR/Cas cargo to the retina using nanoparticles: current possibilities, challenges, and limitations

The discovery of the CRISPR/Cas system and its development into a powerful genome engineering tool have revolutionized the field of molecular biology and generated excitement for its potential to treat a wide range of human diseases. As a gene therapy target, the retina offers many advantages over o...

Deskribapen osoa

Xehetasun bibliografikoak
Egile Nagusiak: Salman, A, Kantor, A, McClements, ME, Marfany, G, Trigueros, S, MacLaren, RE
Formatua: Journal article
Hizkuntza:English
Argitaratua: MDPI 2022