Non-viral delivery of CRIPSR/Cas cargo to the retina using nanoparticles: current possibilities, challenges, and limitations
The discovery of the CRISPR/Cas system and its development into a powerful genome engineering tool have revolutionized the field of molecular biology and generated excitement for its potential to treat a wide range of human diseases. As a gene therapy target, the retina offers many advantages over o...
Egile Nagusiak: | , , , , , |
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Formatua: | Journal article |
Hizkuntza: | English |
Argitaratua: |
MDPI
2022
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