Non-viral delivery of CRIPSR/Cas cargo to the retina using nanoparticles: current possibilities, challenges, and limitations
The discovery of the CRISPR/Cas system and its development into a powerful genome engineering tool have revolutionized the field of molecular biology and generated excitement for its potential to treat a wide range of human diseases. As a gene therapy target, the retina offers many advantages over o...
Main Authors: | Salman, A, Kantor, A, McClements, ME, Marfany, G, Trigueros, S, MacLaren, RE |
---|---|
Format: | Journal article |
Language: | English |
Published: |
MDPI
2022
|
Similar Items
-
Non-Viral Delivery of CRISPR/Cas Cargo to the Retina Using Nanoparticles: Current Possibilities, Challenges, and Limitations
by: Ahmed Salman, et al.
Published: (2022-09-01) -
Minicircle delivery to the neural retina as a gene therapy approach
by: Staurenghi, F, et al.
Published: (2022) -
Insights on the regeneration potential of Müller glia in the mammalian retina
by: Salman, A, et al.
Published: (2021) -
Minicircle Delivery to the Neural Retina as a Gene Therapy Approach
by: Federica Staurenghi, et al.
Published: (2022-10-01) -
RNA editing for Usher syndrome using CRISPR-Cas13
by: Fry, LE, et al.
Published: (2020)