Protocol paper: a multi-center, double-blinded, randomized, 6-month, placebo-controlled study followed by 12-month open label extension to evaluate the safety and efficacy of Saracatinib in Fibrodysplasia Ossificans Progressiva (STOPFOP)

<strong>Background<br></strong> Fibrodysplasia Ossificans Progressiva (FOP) is a genetic, progressive and devastating disease characterized by severe heterotopic ossification (HO), loss of mobility and early death. There are no FDA approved medications. The STOPFOP team identified...

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Bibliographic Details
Main Authors: Smilde, BJ, Stockklausner, C, Keen, R, Whittaker, A, Bullock, AN, von Delft, A, van Schoor, NM, Yu, PB, Eekhoff, EMW
Format: Journal article
Language:English
Published: BioMed Central 2022