Towards an engineered autologous cellular therapy for RAG2 deficiency

<p>Severe combined immune deficiency (SCID) caused by RAG deficiency is a genetically-determined immune deficiency characterized by the virtual absence of adaptive immune cells. Unless treated with a hematopoietic stem cell transplantation (HSCT), RAG deficient patients succumb to severe infec...

Cijeli opis

Bibliografski detalji
Glavni autor: Gardner, CL
Daljnji autori: Acuto, O
Format: Disertacija
Jezik:English
Izdano: 2020
Teme: