Towards an engineered autologous cellular therapy for RAG2 deficiency

<p>Severe combined immune deficiency (SCID) caused by RAG deficiency is a genetically-determined immune deficiency characterized by the virtual absence of adaptive immune cells. Unless treated with a hematopoietic stem cell transplantation (HSCT), RAG deficient patients succumb to severe infec...

Полное описание

Библиографические подробности
Главный автор: Gardner, CL
Другие авторы: Acuto, O
Формат: Диссертация
Язык:English
Опубликовано: 2020
Предметы: