Cystic fibrosis transmembrane conductance regulator (CFTR)-targeted therapeutics for cystic fibrosis
Treatment of the common life-limiting genetic disease cystic fibrosis (CF) has been transformed by small molecule therapeutics that target the root cause of the disease, pathogenic variants in the ATP-binding cassette transporter cystic fibrosis transmembrane conductance regulator (CFTR). Here, we s...
| Main Authors: | , , , , , , , , , |
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| Other Authors: | |
| Format: | Book section |
| Language: | English |
| Published: |
Springer
2024
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