Long-term data with idebenone on respiratory function outcomes in patients with Duchenne muscular dystrophy

Long-term data with idebenone on respiratory function outcomes in patients with Duchenne muscular dystrophy

Decline in respiratory function in patients with DMD starts during early teenage years and leads to early morbidity and mortality. Published evidence of efficacy for idebenone on respiratory function outcomes is currently limited to 12 months of follow-up time. Here we report data collected as retro...

Disgrifiad llawn

Manylion Llyfryddiaeth
Prif Awduron:	Servais, L, Straathof, CSM, Schara, U, Klein, A, Leinonen, M, Hasham, S, Meier, T, De Waele, L, Gordish-Dressman, H, McDonald, CM, Mayer, OH, Voit, T, Mercuri, E, Buyse, GM
Fformat:	Journal article
Iaith:	English
Cyhoeddwyd:	Elsevier 2019

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