The novel role of the B-cell lymphoma/leukemia 11A (BCL11A) gene in β-thalassaemia treatment
β-thalassaemia is a genetic disorder resulting in a reduction or absence of β-globin gene expression. Due to the high prevalence of β-thalassaemia and the lack of available treatment other than blood transfusion and haematopoietic stem cell (HSC) transplantation, the disease represents a considerabl...
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Bentham Science Publishers
2023
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