Targeting RNA to treat neuromuscular disease.

Targeting RNA to treat neuromuscular disease.

The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...

書目詳細資料
Main Authors:	Muntoni, F, Wood, M
格式:	Journal article
語言:	English
出版:	2011

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