Targeting RNA to treat neuromuscular disease.

The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...

Celý popis

Podrobná bibliografie
Hlavní autoři: Muntoni, F, Wood, M
Médium: Journal article
Jazyk:English
Vydáno: 2011