Targeting RNA to treat neuromuscular disease.
The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...
Prif Awduron: | , |
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Fformat: | Journal article |
Iaith: | English |
Cyhoeddwyd: |
2011
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