Targeting RNA to treat neuromuscular disease.

The development of effective therapies for neuromuscular disorders such as Duchenne muscular dystrophy (DMD) is hampered by considerable challenges: skeletal muscle is the most abundant tissue in the body, and many neuromuscular disorders are multisystemic conditions. However, despite these barriers...

Полное описание

Библиографические подробности
Главные авторы: Muntoni, F, Wood, M
Формат: Journal article
Язык:English
Опубликовано: 2011